Abstract

Transcriptional targeting facilitates spatial, inducible or physiologically regulated gene therapy or virotherapy by the utilization of regulatory DNA sequences to drive expression of therapeutic or viral genes. Specific, effective, and vector-compatible promoters are key to the realization of the full potential of transcriptional targeting. Few promoters that fulfill these requirements have been described and for some applications suitable natural promoters might not exist. This chapter reviews strategies developed to overcome these limitations: optimization of natural promoters, design of artificial promoters, and adaptation of vector backbones. These endeavors aim to develop advanced vectors required for future clinical applications.

Original languageEnglish
Title of host publicationVector Targeting for Therapeutic Gene Delivery
Publisherwiley
Pages481-503
Number of pages23
ISBN (Electronic)9780471234302
ISBN (Print)9780471434795
DOIs
StatePublished - Jan 1 2003

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