Onasemnogene abeparvovec for presymptomatic infants with three copies of SMN2 at risk for spinal muscular atrophy: the Phase III SPR1NT trial
- Kevin A. Strauss
- , Michelle A. Farrar
- , Francesco Muntoni
- , Kayoko Saito
- , Jerry R. Mendell
- , Laurent Servais
- , Hugh J. McMillan
- , Richard S. Finkel
- , Kathryn J. Swoboda
- , Jennifer M. Kwon
- , Craig M. Zaidman
- , Claudia A. Chiriboga
- , Susan T. Iannaccone
- , Jena M. Krueger
- , Julie A. Parsons
- , Perry B. Shieh
- , Sarah Kavanagh
- , Melissa Wigderson
- , Sitra Tauscher-Wisniewski
- , Bryan E. McGill
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