Nonclinical evaluation of CNS-administered TPP1 enzyme replacement in canine CLN2 neuronal ceroid lipofuscinosis

Brian R. Vuillemenot, Derek Kennedy, Jonathan D. Cooper, Andrew M.S. Wong, Sarmi Sri, Thom Doeleman, Martin L. Katz, Joan R. Coates, Gayle C. Johnson, Randall P. Reed, Eric L. Adams, Mark T. Butt, Donald G. Musson, Joshua Henshaw, Steve Keve, Rhea Cahayag, Laurie S. Tsuruda, Charles A. O'Neill

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Keyphrases

Biochemistry, Genetics and Molecular Biology

Pharmacology, Toxicology and Pharmaceutical Science

Neuroscience