Nonclinical evaluation of CNS-administered TPP1 enzyme replacement in canine CLN2 neuronal ceroid lipofuscinosis
Brian R. Vuillemenot, Derek Kennedy, Jonathan D. Cooper, Andrew M.S. Wong, Sarmi Sri, Thom Doeleman, Martin L. Katz, Joan R. Coates, Gayle C. Johnson, Randall P. Reed, Eric L. Adams, Mark T. Butt, Donald G. Musson, Joshua Henshaw, Steve Keve, Rhea Cahayag, Laurie S. Tsuruda, Charles A. O'Neill
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