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Neonatal retroviral vector-mediated hepatic gene therapy reduces bone, joint, and cartilage disease in mucopolysaccharidosis VII mice and dogs

  • Robert L. Mango
  • , Lingfei Xu
  • , Mark S. Sands
  • , Carole Vogler
  • , Gabriela Seiler
  • , Tobias Schwarz
  • , Mark E. Haskins
  • , Katherine Parker Ponder

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Veterinary Science and Veterinary Medicine