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Dive into the research topics of 'Liver-directed neonatal gene therapy prevents cardiac, bone, ear, and eye disease in mucopolysaccharidosis I mice'. Together they form a unique fingerprint.- Sort by
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Yuli Liu, Lingfei Xu, Anne K. Hennig, Attila Kovacs, Annabel Fu, Sarah Chung, David Lee, Bin Wang, Ramin S. Herati, Judith Mosinger Ogilvie, Shi Rong Cai, Katherine Parker Ponder
Research output: Contribution to journal › Article › peer-review