Intrathecal enzyme replacement therapy reduces lysosomal storage in the brain and meninges of the canine model of MPS I

E. Kakkis, M. McEntee, C. Vogler, S. Le, B. Levy, P. Belichenko, W. Mobley, P. Dickson, S. Hanson, M. Passage

Research output: Contribution to journalConference articlepeer-review

155 Scopus citations

Fingerprint

Dive into the research topics of 'Intrathecal enzyme replacement therapy reduces lysosomal storage in the brain and meninges of the canine model of MPS I'. Together they form a unique fingerprint.

Medicine & Life Sciences

Chemical Compounds