Increased phosphorylation of HexM improves lysosomal uptake and potential for managing GM2 gangliosidoses

Graeme Benzie, Kristen Bouma, Taylor Battellino, Steven Cooper, Rick Hemming, Wafa Kammouni, Lin Liu, Cuong Do, Mazdak Khajehpour, Helene Perreault, Stuart Kornfeld, Barbara Triggs-Raine, Brian L. Mark

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Biochemistry, Genetics and Molecular Biology