Improved retroviral vector design results in sustained expression after adult gene therapy in mucopolysaccharidosis I mice

Ramin Sedaghat Herati, Xiucui Ma, Mindy Tittiger, Kevin K. Ohlemiller, Attila Kovacs, Katherine P. Ponder

Research output: Contribution to journalArticlepeer-review

27 Scopus citations

Fingerprint

Dive into the research topics of 'Improved retroviral vector design results in sustained expression after adult gene therapy in mucopolysaccharidosis I mice'. Together they form a unique fingerprint.

Medicine & Life Sciences

Chemical Compounds