Has gene therapy for ALS arrived?

Timothy M. Miller, Don W. Cleveland

Research output: Contribution to journalShort surveypeer-review

11 Scopus citations


Amyotrophic lateral sclerosis has not responded well in clinical trials to what initially seemed a promising therapy-the administration of neuronal growth and survival factors. Now, a gene therapy-based approach in mice revives hope that proper delivery of such factors can slow the disease's course.

Original languageEnglish
Pages (from-to)1256-1257
Number of pages2
JournalNature medicine
Issue number10
StatePublished - Oct 2003


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