Has gene therapy for ALS arrived?

Timothy M. Miller; Don W. Cleveland

doi:10.1038/nm1003-1256

Has gene therapy for ALS arrived?

Timothy M. Miller, Don W. Cleveland

Research output: Contribution to journal › Short survey › peer-review

11 Scopus citations

Abstract

Amyotrophic lateral sclerosis has not responded well in clinical trials to what initially seemed a promising therapy-the administration of neuronal growth and survival factors. Now, a gene therapy-based approach in mice revives hope that proper delivery of such factors can slow the disease's course.

Original language	English
Pages (from-to)	1256-1257
Number of pages	2
Journal	Nature medicine
Volume	9
Issue number	10
DOIs	https://doi.org/10.1038/nm1003-1256
State	Published - Oct 2003

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10.1038/nm1003-1256

Cite this

@article{3f2cd8a981a94e1c946555ff45d5f8ea,

title = "Has gene therapy for ALS arrived?",

abstract = "Amyotrophic lateral sclerosis has not responded well in clinical trials to what initially seemed a promising therapy-the administration of neuronal growth and survival factors. Now, a gene therapy-based approach in mice revives hope that proper delivery of such factors can slow the disease's course.",

author = "Miller, {Timothy M.} and Cleveland, {Don W.}",

year = "2003",

month = oct,

doi = "10.1038/nm1003-1256",

language = "English",

volume = "9",

pages = "1256--1257",

journal = "Nature medicine",