Gene therapy for ocular problems in mucopolysaccharidosis: An experimental and promising approach with benefits in animal models - a review

Keyphrases

• Gene Therapy 100%
• Photosystem II 100%
• Ocular Problems 100%
• Hematopoietic Stem Cell Transplantation 20%
• Novel Therapeutics 20%
• Potential Gains 20%
• Enzyme Replacement Therapy 20%
• Viral Vectors 20%
• Leber Congenital Amaurosis 20%
• Visual Function 20%
• Clinical Testing 20%
• Gene Transduction 20%
• Ocular Manifestations 20%
• Recent Introduction 20%
• Inherited Retinal Disease 20%
• Local Gene Therapy 20%
• Systemic Gene Therapy 20%
• Ocular Features 20%
• Human Givens 20%

Medicine and Dentistry

• Mucopolysaccharidosis 100%
• Gene Therapy 100%
• Hematopoietic Stem Cell Transplantation 20%
• Enzyme Replacement Therapy 20%
• Retina Disease 20%
• Virus Vector 20%
• Vision 20%
• Leber Congenital Amaurosis 20%
• Genetic Transduction 20%

Pharmacology, Toxicology and Pharmaceutical Science

• Mucopolysaccharidosis 100%
• Replacement Therapy 20%
• Preclinical Study 20%
• Retina Disease 20%
• Viral Vector 20%
• Leber Congenital Amaurosis 20%