Enhanced Efficacy and Increased Long-Term Toxicity of CNS-Directed, AAV-Based Combination Therapy for Krabbe Disease
- Yedda Li
- , Christopher A. Miller
- , Lauren K. Shea
- , Xuntian Jiang
- , Miguel A. Guzman
- , Randy J. Chandler
- , Sai M. Ramakrishnan
- , Stephanie N. Smith
- , Charles P. Venditti
- , Carole A. Vogler
- , Daniel S. Ory
- , Timothy J. Ley
- , Mark S. Sands
- Institute of Clinical and Translational Sciences (ICTS)
- Siteman Cancer Center
- Division of Endocrinology, Metabolism & Lipid Research
- Roy and Diana Vagelos Division of Biology & Biomedical Sciences (DBBS)
- Center of Regenerative Medicine
- Bursky Center for Human Immunology and Immunotherapy
- Division of Oncology
- Section of Stem Cell Biology
- DBBS - Immunology
- DBBS - Molecular Genetics and Genomics
- DBBS - Molecular Cell Biology
- DBBS - Neurosciences
- DBBS - Cancer Biology
- Hope Center for Neurological Disorders
- Intellectual and Developmental Disabilities Research Center (IDDRC)
Research output: Contribution to journal › Article › peer-review
46
Link opens in a new tab
Scopus
citations