Cholesterol homeostatic responses provide biomarkers for monitoring treatment for the neurodegenerative disease Niemann-Pick C1 (NPC1)

Brett Tortelli, Hideji Fujiwara, Jessica H. Bagel, Jessie Zhang, Rohini Sidhu, Xuntian Jiang, Nicole M. Yanjanin, Roopa Kanakatti Shankar, Nuria Carillo-Carasco, John Heiss, Elizabeth Ottinger, Forbes D. Porter, Jean E. Schaffer, Charles H. Vite, Daniel S. Ory

Research output: Contribution to journalArticlepeer-review

36 Scopus citations

Fingerprint

Dive into the research topics of 'Cholesterol homeostatic responses provide biomarkers for monitoring treatment for the neurodegenerative disease Niemann-Pick C1 (NPC1)'. Together they form a unique fingerprint.

Keyphrases

Medicine and Dentistry

Pharmacology, Toxicology and Pharmaceutical Science

Biochemistry, Genetics and Molecular Biology

Neuroscience