AAV-mediated intravitreal gene therapy reduces lysosomal storage in the retinal pigmented epithelium and improves retinal function in adult MPS VII mice

Anne K. Hennig, Judith Mosinger Ogilvie, Kevin K. Ohlemiller, Adrian M. Timmers, William W. Hauswirth, Mark S. Sands

Research output: Contribution to journal › Article › peer-review

16 Scopus citations

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Medicine & Life Sciences

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