Network

King's College London

External organization: Academic

Natalie Fund

External organization: Unknown

Lincoln University

External organization: Academic

Harvard University

External organization: Academic

Stanford University

External organization: Academic

University of Hamburg

External organization: Academic

University of Oxford

External organization: Academic

NCL Stiftung

External organization: Unknown

Folkhalsan

External organization: Unknown

Sanford Health

External organization: Medical

Medical Research Council

External organization: Government

University of Bristol

External organization: Academic

Charles University

External organization: Academic

Amicus Therapeutics

External organization: Unknown

Iowa State University

External organization: Academic

Regenexbio Inc.

External organization: Unknown

Saoirse Foundation

External organization: Unknown

Hamill Foundation

External organization: Unknown

Johnson & Johnson

External organization: Corporate

McGill University

External organization: Academic

NHS Lothian

External organization: Medical

Genzyme Corporation

External organization: Corporate

European Commission

External organization: Academic

University of Exeter

External organization: Academic

University of Iowa

External organization: Academic

Remy foundation

External organization: Unknown

Abeona Therapeutics

External organization: Unknown

Saint Louis University

External organization: Academic

Kiel University

External organization: Academic

University of Dundee

External organization: Academic

GlaxoSmithKline

External organization: Corporate

Wellcome Trust

External organization: Academic

Sanofi-Aventis

External organization: Corporate

Allievex Corporation

External organization: Unknown

University of Szeged

External organization: Academic

EJLB Foundation

External organization: Unknown

BDSRA-US

External organization: Unknown

Bielefeld University

External organization: Academic

University of Otago

External organization: Academic

Gauchers Association

External organization: Unknown

FIMM

External organization: Unknown

Roslin Institute

External organization: Unknown

FP7/2007

External organization: Unknown

REGENXBIO Inc.

External organization: Corporate

University of Glasgow

External organization: Academic

Merck

External organization: Corporate

Bletsoe Family

External organization: Unknown

Uppsala University

External organization: Academic

Hailey's Heroes

External organization: Unknown

Peto Foundation

External organization: Unknown

StageBio

External organization: Unknown

Sparks Foundation

External organization: Unknown

Keele University

External organization: Academic

University of Oslo

External organization: Academic

Phoenix Nest Inc.

External organization: Unknown

Aarhus University

External organization: Academic

University of Cologne

External organization: Academic

Fondazione Telethon

External organization: Unknown

DAP

External organization: Unknown

Rutgers University

External organization: Unknown

University of Sussex

External organization: Academic

SNRP

External organization: Unknown

Polytechnique Montreal

External organization: Academic

IIBBA-CONICET

External organization: Unknown

JNCL

External organization: Unknown

Cornell University

External organization: Academic

Hearst Foundations

External organization: Unknown

University of Kansas

External organization: Academic

Research Councils UK

External organization: Unknown

University of Adelaide

External organization: Academic

Leiden University

External organization: Academic

Alnylam

External organization: Unknown

University of Florida

External organization: Academic

Ohio State University

External organization: Academic

Sorbonne Université

External organization: Academic

colony

External organization: Unknown

University of Toronto

External organization: Academic

University of Leeds

External organization: Academic

Alfaisal University

External organization: Academic

NHS

External organization: Unknown

Roslin Foundation

External organization: Unknown

NINDS R01NS039995

External organization: Unknown

Cardiff University

External organization: Academic

University of Montreal

External organization: Academic

Lund University

External organization: Academic

Stem Cells Inc.

External organization: Unknown

Sanford Research

External organization: Unknown

Maastricht University

External organization: Academic

University of Missouri

External organization: Academic

Cecilia Ljungberg

External organization: Unknown

NIH

External organization: Unknown

Royal Society

External organization: Unknown

Pratt Foundation

External organization: Unknown

KU Leuven

External organization: Academic

Lab 3510

External organization: Unknown

Niemann-Pick UK

External organization: Unknown

University of Bonn

External organization: Academic

Haley’s Heroes

External organization: Unknown